Cystic Fibrosis
Cystic Fibrosis Market

Cystic Fibrosis is a life-limiting autosomal recessive genetic disorder that severely damages the lungs and the digestive system. 


This disease is caused by a genetic mutation in the CFTR gene. The CFTR protein is a chloride-conducting trans-membrane conductance regulator and is called cystic fibrosis transmembrane conductance regulator. The mutation is autosomal recessive, which implies that the gene is not on the sex chromosome, and the symptoms would manifest only when both the alleles are mutated for the gene.

Cystic Fibrosis Epidemiological Segmentation 

The Epidemiological Segmentation of Cystic Fibrosis in 6MM from 2017 to 2030 is segmented as:- 

  • Total prevalent cases
  • Gender-specific cases
  • Age-specific cases
  • Type-specific cases

Cystic Fibrosis Epidemiology 

  • Total Cystic Fibrosis prevalent population in 6MM in 2017 was 61,306  
  • The prevalent population of Cystic Fibrosis in the United States was 30,139 in 2017  
  • Gender-Specific cases in the US for Females, it was observed to be 14,587 cases, whereas, for Males, it was 15,552 cases in 2017. 

Cystic Fibrosis Market

Cystic Fibrosis Market Size in 6MM was USD 1,940.1 million in 2017.

Cystic Fibrosis Market Drivers

  • The high number of drugs in the pipeline
  • Better diagnostic techniques
  • Most frequent mutation
  • Increased Research Funding

Cystic Fibrosis Market Barriers

  • Cost of treatment
  • Rarity of Disease
  • Future competition

Cystic Fibrosis Emerging Drugs

The emerging drugs of the Cystic Fibrosis market are 

  • MRT5005
  • Nesolicaftor (PTI-428)
  • Dirocaftor (PTI-808)
  • VX-121
  • ARO-ENaC
  • Eluforsen
  • IONIS-ENaC-2.5
  • Ensifentrine
  • ELX-02
  • VX-659
  • Posenacaftor (PTI-801)
  • Deutivacaftor (VX-561)

And many others. 

Cystic Fibrosis Key Players

The key players in the Cystic Fibrosis market are

  • Translate Bio, Inc.
  • Proteostasis Therapeutics
  • Vertex Pharmaceuticals, Inc
  • Arrowhead Pharmaceuticals
  • ProQR Therapeutics
  • Ionis Pharmaceuticals
  • Verona Pharmaceuticals
  • Eloxx Pharmaceuticals, Inc

And many others.