Cystinuria Market

• Cystinura market size is expected to grow at a significant CAGR during the study period (2019-2032).
• Cystinuria companies working in the cystinuria market are Retrophin, Inc., Recordati Rare Diseases Inc., Mission Therapeutics Ltd., Enterome Bioscience, Horizon Therapeutics plc, Arcturus Therapeutics Holdings Inc., Codexis, Inc., Mito Pharmaceuticals, Inc., and many Others.
• In January 2025, Advicenne provided update on recent exchanges with the US FDA about the development of ADV7103 in cystinuria, and announced that it has reached an important
• milestone.
• PharmaKrysto is an early-stage research and development company dedicated to improving outcomes for individuals with cystinuria by preserving kidney function and preventing unnecessary pain.

DelveInsight's "Cystinuria Market Insights, Epidemiology, and Market Forecast-2032" report delivers an in-depth understanding of the Cystinuria, historical and forecasted epidemiology as well as the Cystinuria market therapeutics trends in the United States, EU5 (Germany, Spain, Italy, France, and United Kingdom) and Japan.

The Cystinuria market report provides current treatment practices, emerging Cystinuria drugs, Cystinuria market share of the individual Cystinuria therapies, current and forecasted Cystinuria market Size from 2019 to 2032 segmented by seven major markets. The Report also covers current Cystinuria treatment market/algorithm, market drivers, market barriers and unmet medical needs to curate the best of the opportunities and assesses the underlying potential of the Cystinuria market.

Cystinuria Treatment Market

The DelveInsight’s Cystinuria treatment market report gives a thorough understanding of the Cystinuria by including details such as disease definition, symptoms, causes, pathophysiology, diagnosis, and treatment.

Cystinuria Overview

In the kidney, ureter, and bladder, cysteine-based stones can form in a disorder known as cystinuria. When two molecules of the amino acid cysteine are linked together, cysteine is created. Families transmit the condition down across generations.

Cystinuria Diagnosis

This segment of the report covers the detailed diagnostic methods or tests for Cystinuria.

Cystinuria Treatment

It covers the details of conventional and current medical therapies available in the Cystinuria treatment market for the treatment of the condition. It also provides Cystinuria treatment algorithms and guidelines in the United States, Europe, and Japan. Cystinuria clinical trials focus on novel therapies to prevent cystine stone formation. Key studies evaluate tiopronin formulations, gene therapies, and urinary alkalinization strategies to improve long-term outcomes and reduce recurrence.

Cystinuria Epidemiology

The Cystinuria epidemiology section provides insights about the historical and current Cystinuria patient pool and forecasted trends for individual seven major countries. It helps to recognize the causes of current and forecasted trends by exploring numerous studies and views of key opinion leaders. This part of the Cystinuria therapuetics market report also provides the diagnosed patient pool and their trends along with assumptions undertaken. 

Key Findings

The disease epidemiology covered in the report provides historical as well as forecasted Cystinuria epidemiology scenario in the 7MM covering the United States, EU5 countries (Germany, Spain, Italy, France, and the United Kingdom), and Japan from 2019 to 2032.

• According to Leslie et al. (2023), cystinuria is the most common inheritable cause of kidney stone disease. Worldwide and in the US, the overall prevalence is about 1 in 7,000 but varies significantly by population. Prevalence is 1 per
• 100,000 in Sweden, 1 per 18,000 in Japan, 1 per 4,000 in Australia, 1 per 2,500 in Israel, and 1 per 2,000 in Great Britain and Spain.
• The 5-year recurrence rate for cysteine stones is higher than any other stone type at 83%.
• Men are affected about twice as often as women. The peak age of presentation of the first cystine stone is 22 years of age, although 22% of cystinuria patients will start making calculi as children.
• Twenty to forty percent of cystinuria patients have other kidney stone-related urinary chemical abnormalities, such as hypocitraturia (44%), hypercalciuria (19%), or hyperuricosuria (22%)

Country Wise- Cystinuria Epidemiology

The epidemiology segment also provides the Cystinuria epidemiology data and findings across the United States, EU5 (Germany, France, Italy, Spain, and the United Kingdom), and Japan.

Cystinuria Drug Chapters

The drug chapter segment of the Cystinuria treatment market report encloses the detailed analysis of Cystinuria marketed drugs and late-stage (Phase-III and Phase-II) Cystinuria pipeline drugs. It also helps to understand the Cystinuria clinical trials details, expressive pharmacological action, agreements and collaborations, approval and patent details, advantages and disadvantages of each included drug and the latest news and press releases. The Cystinuria drugs market is driven by increasing awareness and demand for effective therapies. Key treatments include tiopronin and potassium citrate, with companies like Retrophin and Exela Pharma active in development.

Cystinuria Marketed Drugs

The report provides the details of the marketed products/off-label treatments available for Cystinuria treatment market.

Cystinuria Emerging Drugs

The report provides the details of the emerging therapies under the late and mid-stage of development for Cystinuria treatment.

Cystinuria Market Outlook

The Cystinuria therapeutics market outlook of the report helps to build a detailed comprehension of the historic, current, and forecasted Cystinuria market trends by analyzing the impact of current Cystinuria therapies on the market, unmet needs, drivers and barriers, and demand for better technology.

This segment gives a thorough detail of Cystinuria market trend of each marketed drug and late-stage pipeline therapy by evaluating their impact based on the annual cost of therapy, inclusion and exclusion criteria's, Cystinuria mechanism of action, compliance rate, growing need of the market, increasing patient pool, covered patient segment, expected launch year, competition with other therapies, brand value, their impact on the market and view of the key opinion leaders. The calculated Cystinuria market data are presented with relevant tables and graphs to give a clear view of the market at first sight.

According to DelveInsight, the Cystinuria market in 7MM is expected to witness a major change in the study period 2019-2032.

Key Findings

This section includes a glimpse of the Cystinuria market in 7MM.

The United States Market Outlook

This section provides the total Cystinuria market size and market size by therapies in the United States.

EU-5 Countries: Market Outlook

The total Cystinuria market size and market size by therapies in Germany, France, Italy, Spain, and the United Kingdom is provided in this section.

Japan Market Outlook

The total Cystinuria market size and market size by therapies in Japan is also mentioned.

Cystinuria Drugs Uptake

This section focuses on the rate of uptake of the potential Cystinuria drugs recently launched in the Cystinuria therapies market or expected to get launched in the market during the study period 2019-2032. The analysis covers Cystinuria drugs market uptake by drugs; patient uptake by therapies; and sales of each drug.   

Cystinuria Drugs Uptake helps in understanding the drugs with the most rapid uptake, reasons behind the maximal use of new drugs, and allow the comparison of the drugs on the basis of Cystinuria market share and size which again will be useful in investigating factors important in market uptake and in making financial and regulatory decisions.

Cystinuria Pipeline Development Activities

The Cystinuria report provides insights into Cystinuria Clinical Trials within in Phase II, and Phase III stage. It also analyses Cystinuria key players involved in developing targeted therapeutics.

Pipeline Development Activities

The Cystinuria treatment market report covers the detailed information of collaborations, acquisition, and merger, licensing, patent details, and other information for Cystinuria emerging therapies.

Reimbursement Scenario in Cystinuria

Approaching reimbursement proactively can have a positive impact both during the late stages of product development and well after product launch. In a report, we take reimbursement into consideration to identify economically attractive indications and market opportunities. When working with finite resources, the ability to select the markets with the fewest reimbursement barriers can be a critical business and price strategy.

KOL- Views

To keep up with current Cystinuria market trends, we take KOLs and SMEs ' opinion working in the Cystinuria domain through primary research to fill the data gaps and validate our secondary research. Their opinion helps to understand and validate current and emerging therapies treatment patterns or Cystinuria market trends. This will support the clients in potential upcoming novel treatment by identifying the overall scenario of the market and the unmet needs.

Competitive Intelligence Analysis

We perform Competitive and Market Intelligence analysis of the Cystinuria Market by using various Competitive Intelligence tools that include - SWOT analysis, PESTLE analysis, Porter's five forces, BCG Matrix, Market entry strategies etc. The inclusion of the analysis entirely depends upon the data availability.

Scope of the Cystinuria Market Report

• The report covers the descriptive overview of Cystinuria, explaining its causes, signs and symptoms, pathophysiology, diagnosis and currently available therapies
• Comprehensive insight has been provided into the Cystinuria epidemiology and treatment in the 7MM
• Additionally, an all-inclusive account of both the current and emerging therapies for Cystinuria is provided, along with the assessment of new therapies, which will have an impact on the current treatment landscape
• A detailed review of the Cystinuria market; historical and forecasted is included in the report, covering drug outreach in the 7MM
• The report provides an edge while developing business strategies, by understanding trends shaping and driving the global Cystinuria market

Cystinuria Market Report Highlights

• In the coming years, the Cystinuria market is set to change due to the rising awareness of the disease, and incremental healthcare spending across the world; which would expand the size of the market to enable the drug manufacturers to penetrate more into the market
• The Cystinuria companies and academics are working to assess challenges and seek opportunities that could influence Cystinuria R&D. The therapies under development are focused on novel approaches to treat/improve the disease condition      
• Major players are involved in developing therapies for Cystinuria. The launch of emerging therapies will significantly impact the Cystinuria market
• A better understanding of disease pathogenesis will also contribute to the development of novel therapeutics for Cystinuria
• Our in-depth analysis of the pipeline assets across different stages of development (Phase III and Phase II), different emerging trends and comparative analysis of pipeline products with detailed Cystinuria clinical trials, key cross-competition, launch date along with product development activities will support the clients in the decision-making process regarding their therapeutic portfolio by identifying the overall scenario of the research and development activities

Cystinuria Report Insights

• Cystinuria Patient Population
• Cystinuria Therapeutic Approaches
• Cystinuria Pipeline Analysis
• Cystinuria Market Size and Trends
• Cystinuria Market Opportunities
• Impact of upcoming Cystinuria Therapies

Cystinuria Report Key Strengths

• 10 Years Forecast
• 7MM Coverage
• Cystinuria Epidemiology Segmentation
• Key Cross Competition
• Highly Analyzed Market
• Cystinuria Drugs Uptake

Cystinuria Report Assessment

• Current Cystinuria Treatment Practices
• Cystinuria Unmet Needs
• Cystinuria Pipeline Product Profiles
• Cystinuria Market Attractiveness
• Cystinuria Market Drivers
• Cystinuria Market Barriers

Key Questions Cystinuria Market Report:

Cystinuria Market Insights:

• What was the Cystinuria drug class share (%) distribution in 2019 and how it would look like in 2032?
• What would be the Cystinuria total market size as well as market size by therapies across the 7MM during the forecast period (2019-2032)?
• What are the key findings pertaining to the market across 7MM and which country will have the largest Cystinuria market size during the forecast period (2019-2032)?
• At what CAGR, the Cystinuria market is expected to grow by 7MM during the forecast period (2019-2032)?
• What would be the Cystinuria market outlook across the 7MM during the forecast period (2019-2032)?
• What would be the Cystinuria market growth till 2032, and what will be the resultant market Size in the year 2032?
• How would the unmet needs affect the market dynamics and subsequent analysis of the associated trends?

Cystinuria Epidemiology Insights:

• What are the disease risk, burden, and regional/ethnic differences of the Cystinuria?
• What are the key factors driving the epidemiology trend for seven major markets covering the United States, EU5 (Germany, Spain, France, Italy, UK), and Japan?
• What is the historical Cystinuria patient pool in seven major markets covering the United States, EU5 (Germany, Spain, France, Italy, UK), and Japan?
• What would be the forecasted patient pool of Cystinuria in seven major markets covering the United States, EU5 (Germany, Spain, France, Italy, UK), and Japan?
• Where will be the growth opportunities in the 7MM with respect to the patient population pertaining to Cystinuria?
• Out of all 7MM countries, which country would have the highest prevalent population of Cystinuria during the forecast period (2019-2032)?
• At what CAGR the patient population is expected to grow in 7MM during the forecast period (2019-2032)?

Current Cystinuria Treatment Scenario, Marketed Drugs and Emerging Therapies:

• What are the current options for the Cystinuria treatment in addition to the approved therapies?
• What are the current treatment guidelines for the treatment of Cystinuria in the USA, Europe, and Japan?
• What are the Cystinuria marketed drugs and their respective MOA, regulatory milestones, product development activities, advantages, disadvantages, safety and efficacy, etc.?
• How many Cystinuria companies are developing therapies for the treatment of Cystinuria?
• How many therapies are in-development by each company for Cystinuria treatment?
• How many are emerging therapies in mid-stage, and late stage of development for Cystinuria treatment?
• What are the key collaborations (Industry - Industry, Industry - Academia), Mergers and acquisitions, licensing activities related to the Cystinuria therapies?
• What are the recent novel therapies, targets, Cystinuria mechanisms of action and technologies being developed to overcome the limitation of existing therapies?
• What are the Cystinuria clinical trials going on for Cystinuria and their status?
• What are the current challenges faced in drug development?
• What are the key designations that have been granted for the emerging therapies for Cystinuria?
• What are the global historical and forecasted market of Cystinuria?

Reasons to buy Cystinuria Market Forecast Report

• The report will help in developing business strategies by understanding trends shaping and driving the Cystinuria market
• To understand the future market competition in the Cystinuria market and Insightful review of the key market drivers and barriers
• Organize sales and marketing efforts by identifying the best opportunities for Cystinuria in the US, Europe (Germany, Spain, Italy, France, and the United Kingdom) and Japan
• Identification of strong upcoming players in the market will help in devising strategies that will help in getting ahead of competitors
• Organize sales and marketing efforts by identifying the best opportunities for Cystinuria market
• To understand the future market competition in the Cystinuria market