The US FDA for the third time has refused to give approval to Lipocine’s oral testosterone drug, Tlando. The drug is an oral testosterone replacement therapy in clinical trials for the treatment of...
Sanfilippo syndrome, also known as mucopolysaccharidosis type III (MPS III), is a rare genetic disorder that affects the Central Nervous system. It is a result of a mutation in genes and can be of four types (A, B, C, and D). In all the four cases, the body fails to clear up the toxic sugars such as mucopolysacchar...
Find MoreDown Syndrome Awareness Month Every year, October is observed as World Down Syndrome awareness month, aiming to aware the general population about Down syndrome. It is a genetic disorder, also known as Trisomy 21 that is caused by the presence of partial or complete of a third copy of a chromosome 21. The early ...
Find MoreBatten disease overview Batten disease, referred to as Neuronal Ceroid Lipofuscinosis (NCL), is a family of rare diseases and a debilitating autosomal recessive neurodegenerative lysosomal storage disorder caused by cellular accumulation of abnormal auto-fluorescent lipoproteins lipofuscin. Patients with Batt...
Find MoreFlagship Pioneering has launched Omega Therapeutics with an aim to take forward the genomic medicine. The launch of Omega therapeutics was planned to focus on epigenetic drugs to target diseases. Study of changes in gene expressions without any changes in the DNA sequence is known as Epigenetics. This oft...
Find MoreSpinal Muscular Atrophy is a rare and the second most fatal autosomal recessive genetic disorder with an incidence of 1 in 6000 to 1 in 10,000 births. Globally talking, SMA prevalence was reported in 19,343 cases in the year 2017 in the 7MM, and the US accounted for the highest number of cases approximately around ...
Find MoreNiemann–Pick disease type C (NPC) is a rare genetic disorder which progress and worsens with time. Affecting males and females, DelveInsight estimated the total Niemann–Pick disease type C prevalent population in the 7MM around 2116 in 2017, and the total diagnosed NPC prevalent population was observed to be 1,058....
Find MoreCHMP opines positively for 13 Drugs for a variety of disease The Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has endorsed the use of 13 medicinal drugs for a variety of indications. These include five new medications and eight existing ones whose use is extended ...
Find MoreAI-powered drug-maker Recursion Pharmaceuticals secures USD 121 M to accelerate its clinical programs Recursion Pharmaceuticals, a next-gen biopharma company, has raised USD 121 Million in Series C financing. The Series C round was led by Baillie Gifford's flagship investment trust, Scottish Mortgage Investment...
Find MoreThe era, we are living in has experienced many advancements in the healthcare system. Curative, and life-changing gene therapies have started to promise a future free of prolonged illness, possessing an ability to treat, cure or ease the life-draining diseases. In a major event, the approval of the other gene t...
Find MoreWith its innovative approach, chimeric antigen receptor T cell therapy created a new dawn in the age.....
Find MoreToll-like Receptors (TLRs) are a type of pattern recognition receptor (PRR) that recognizes pathogen.....
Find MoreMajor Depressive Disorder (MDD), also known as clinical depression, is a severe, debilitating and fr.....
Find MoreAn autosomal metabolic disorder – Pompe disease results in deterioration of organs and tissues as .....
Find MoreXerostomia is a condition characterized by dry mouth, which is a result of a reduced or absent flow .....
Find MoreIt was assumed initially that Alzheimer’s Disease was a rare condition, but now it is considered t.....
Find MoreThe American Society of Clinical Oncology (ASCO) is one of the largest and most respected conferences in the field of oncology. Held annually, this conference brings together researchers, physicians, and other healthcare professionals from around the world to discuss the latest advances in cancer research, diagnosis, and treatment.