The Evolved Gene Therapy for Hemophilia

Cell and Gene Therapy

Navigating the Vital Role of Bioinformatics in ...

Bioinformatics is one of the healthcare industry's most spotlighted and trending topics today. The Bioinformatics market is evolving rapidly and reaching new heights with each passing day, leading ...

Dec 07, 2022

Pharma News for Zealand Pharma, Amylyx, Sarepta
Zealand Pharma’s Phase III Results of Glepaglutide; FDA Approves Amylyx’s ALS Drug Relyvrio; Novo Nordisk and Ventus Therapeutics Signs Licencing Deal; FDA Approves Futibatinib; Sarepta Files Duchenne Muscular Dystrophy for FDA Approval; Biogen and Eisai’s Lcanemab Phase III Study

Zealand Pharma Announces the Positive Topline Results from its Phase III trial of Glepaglutide Zealand Pharma A/S, a biotech company specializing in peptide-based medicines, announced positive topline results from its phase III trial of glepaglutide. In the evenly randomized double-blind trial, 106 patients with...

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Wilson’s Disease Presents Unique Challenges and Demand for Novel Treatment Therapies

Wilson’s disease is a rare genetic disorder caused by mutations in the P-type ATPase gene. Wilson’s disease causes defective biliary excretion of copper, leading to its accumulation, particularly in the liver and brain. The ATP7B gene is responsible for the transportation of copper from the liver to the intestine t...

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Unraveling the Potential of CRISPR Technology in the Gene-editing Space

CRISPR technology or CRISPR/Cas9 technology is a genome-editing tool derived from the bacterial defense system against viruses and plasmids. The system comprises the Cas9 nuclease enzyme to create site-directed dsDNA (double-stranded DNA) break and a guide RNA, which is a predesigned 20 bp long RNA sequence within ...

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Top Most Expensive Drugs in the US Healthcare Market
Top 12 Most Expensive Drugs in the US Healthcare Market

Drug pricing is one of the hottest topics in the healthcare segment. Several arguments have been put forward by people, governments, healthcare companies, and other organizations in favor of and against expensive medicines. Some of the drugs are so expensive that they are nearly out of reach of the common people. H...

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Pfizer to acquire Arena Pharma; Takeda’s ‘Wave 2’ multiple myeloma med data; Novartis’s next-gen CAR-Ts clinical data; Roche unveils Avenio system

Pfizer acquires drugmaker Arena for USD 6.7 billion to address unmet needs Pfizer declared that it is acquiring Arena Pharmaceuticals, a drug company specializing in inflammation and immunology, for almost USD 7 billion. The pharma giant said it would finance the agreement, worth USD 6.7 billion, with cash on ha...

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CAR-T Cell Therapy aka Miraculous Technology: Mapping the Market, Approved Therapies, Competitive Landscape and Impact of COVID-19

Chimeric antigen receptor T-cell (CAR T) therapies are shown to have transformative potential as a new type of cancer treatment that utilizes the immune system to fight the disease. It involves the process where genetically engineered T cells (patient/donor) express a chimeric antigen receptor to target a specific ...

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Avrobio’s Gene Therapy for Cystinosis Treatment: A New Hope to Overcome the Existing Medical Unmet Needs

Cystinosis is a genetic condition that causes the buildup of the amino acid "cystine" in the cells of the body is known as cystinosis. Due to the excessive accumulation of cystine in various cells, organs, tissues, including the kidneys, eyes, liver, thyroid, muscles, pancreas, brain, and white blood cells of the b...

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The Evolved Gene Therapy for Hemophilia

Hemophilia is an inherited rare disorder where blood doesn’t clot in the regular way because the person affected doesn’t make enough blood-clotting proteins (clotting factors). Without these factors, patients cannot stop bleeding when they are injured. Patients with more severe forms of the disease can experience s...

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Analyzing the Key Companies and the Emerging Gene Therapy in the Dermatology Segment

Advances in genetics research have sparked a surge in interest in gene therapy in dermatology in recent years. Dermatology treatment options have expanded beyond topical drugs to include oral medications, injectables, and light and laser therapy. Now, rather than simply treating symptoms, gene therapy in dermatolog...

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Rheumatoid Arthritis
Rheumatoid Arthritis...

Rheumatoid Arthritis (RA) is a chronic, inflammatory autoimmune disease that leads to progressive an.....

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Toll-like receptors (TLR) 7 and 8 Agonist
Toll-like receptors (TLR)...

Toll-like receptors (TLR) 7 and 8 are functionally localized to endosomes and recognize specific RNA.....

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Gene Therapies
Gene Therapies

Gene therapies are regarded as one of the potential revolution in the Pharmaceutical field and Healt.....

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