Spinal Muscular Atrophy is a rare and the second most fatal autosomal recessive genetic disorder with an incidence of 1 in 6000 to 1 in 10,000…
Tag: Biogen Spinraza
May 27 
Meet the World’s most expensive drug: Zolgensma
The U.S. FDA recently approved the much talked about Novartis’s drug Zolgensma for treating a life-threatening condition Spinal Muscular Atrophy (SMA). SMA is a neuromuscular disorder…
Apr 29 
Spinal Muscular Atrophy: Current and Emerging Therapies
Spinal muscular atrophy (SMA) being a rare genetic neuromuscular disorder results in progressive muscle weakness and atrophy. It affects the part of the nervous system that…
Apr 24 
Can Spinal Muscular Atrophy be treated by Protease Inhibitors?
Spinal muscular atrophy is a genetic disorder characterised by weakness and wasting (atrophy) of skeletal muscles, used for movement. Loss of specialised nerve cells, called motor…
