Sep 06, 2021
Phenylketonuria is an inherited disorder characterized by the absence or deficiency of an enzyme called phenylalanine hydroxylase (PAH), responsible for processing the amino acid phenylalanine. The condition affects one in 13,500 to 19,000 newborns in the United States, says NORD. DelveInsight’s Phenylketonuria epi...
Read More...
Sep 03, 2021
Charcot-Marie-Tooth (CMT) disease is a rare, chronic and sensory neuropathy that causes weakness of the limbs and progresses gradually over time. It can lead to atrophy, sensory loss and complete limb dysfunction. However, rare, the condition is the most common inherited disorder that damages peripheral nerves with...
Read More...
Sep 02, 2021
FDA awards Breakthrough Device Designation to Impella ECP On August 18, 2021, Abiomed received breakthrough device designation from the United States Food and Drug Administration (FDA) for its Impella ECP expandable percutaneous heart pump, the world’s smallest heart pump and the first to be compatible wit...
Read More...
Sep 01, 2021
Drones, also referred to as unmanned aerial vehicles (UAVs)/unpiloted aircraft, are remotely piloted to meet various needs. Drones are one of the emerging technologies that are reshaping the transportation system. Earlier, the main use of drones was for a military expedition, however, today the drones can be seen i...
Read More...
Aug 31, 2021
FDA's Green Flag to Ascendis's Once-Weekly SKYTROFA for Treatment of Pediatric Growth Hormone Deficiency For the treatment of growth failure due to deficiency of growth hormones, the USFDA approved Ascendis Pharma's Skytrofa (lonapegsomatropin-tcgd) for children of one year and older suffering from an improper s...
Read More...
Aug 30, 2021
Venous thromboembolism (VTE) is a condition that is characterized by the development of blood clots in the veins. The condition includes Deep vein thrombosis (DVT) which occurs when a blood clot forms in a deep vein of the lower legs or pelvic area. However, in some cases, the blood clots from pelvic areas may brea...
Read More...
Aug 20, 2024
Duchenne muscular dystrophy (DMD) is a rare genetic disorder usually diagnosed in young boys, gradually weakening muscles across the body until the heart or lungs fail. Symptoms often show up by the age of 5; as the disease progresses, patients tend to lose the ability to walk around the age of 12. As per a recent ...
Read More...
Aug 26, 2021
Shape Therapeutics inks gene therapy deal with Roche worth up to USD 3 Billion Seattle biotech firm Shape Therapeutics has signed a deal potentially exceeding USD 3 billion with pharma giant Roche to bolster the development of gene therapies for Alzheimer’s and Parkinson’s disease. Shape’s RNA editing technol...
Read More...
Aug 25, 2021
Pharmaceutical companies play a vital part in our lives and in helping us to live healthier lives. The pharmaceutical industry finds, develops, manufactures, and promotes medicines or pharmaceutical drugs for usage as medications that are administered (or self-administered) to patients in order to cure, vaccinate, ...
Read More...
Aug 24, 2021
AstraZeneca's Newly Occupied Alexion Hits Rock Bottom After Ultomiris (Ravulizumab) Fails to Show Efficacy in Patients with Amyotrophic Lateral Sclerosis AstraZeneca's 39 billion USD complete acquisition of Alexion took over just a few months back. Unpleasant news strike hard for their first deal in the rare neu...
Read More...