Biogen’s ALS drug Tofersen (BIIB067); Pha...

Phenylketonuria is an inherited disorder characterized by the absence or deficiency of an enzyme called phenylalanine hydroxylase (PAH), responsible for processing the amino acid phenylalanine. The condition affects one in 13,500 to 19,000 newborns in the United States, says NORD. DelveInsight’s Phenylketonuria epi...

FDA awards Breakthrough Device Designation to Impella ECP  On August 18, 2021, Abiomed received breakthrough device designation from the United States Food and Drug Administration (FDA) for its Impella ECP expandable percutaneous heart pump, the world’s smallest heart pump and the first to be compatible wit...

FDA's Green Flag to Ascendis's Once-Weekly SKYTROFA for Treatment of Pediatric Growth Hormone Deficiency For the treatment of growth failure due to deficiency of growth hormones, the USFDA approved Ascendis Pharma's Skytrofa (lonapegsomatropin-tcgd) for children of one year and older suffering from an improper s...

Boston Scientific starts recruitment for randomized controlled trials for the EkoSonic™ Endovascular System On August 04, 2021, Boston Scientific Corporation started the enrolment in the HI-PEITHO clinical trial, which is a collaborative research study with the Pulmonary Embolism Response Team (PERT) Cons...

As per the WHO, “the number of people affected with Diabetes has grown significantly from 108 million in 1980 to 422 million in 2014. A rising trend in prevalence is observed in low- and middle-income countries as compared to high-income countries”. Additionally, Diabetes is a significant cause of the number of dea...

Primary hyperoxaluria (PH) is a rare autosomal genetic form of Hyperoxaluria, a condition that leads to the excessive urinary excretion of oxalate. Till now, three distinct hereditary enzymatic deficiencies have been identified as a cause of PH, namely, PH type 1 (PH1), type 2 (PH2), and type 3 (PH3), with PH1 as t...