exa-cel
Aug 22, 2025
Vertex & CRISPR Therapeutics Make History: FDA Approves exa-cel, the First CRISPR Gene Therapy for Sickle Cell and Beta-Thalassemia
Vertex Pharmaceuticals and CRISPR Therapeutics have become the first companies to secure FDA approval for a CRISPR-based gene-editing therapy. Vertex Pharmaceuticals, in partnership with CRISPR Therapeutics, has achieved a historic milestone with the FDA approval of exagamglogene autotemcel (exa-cel, branded as ...
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Dec 15, 2023
Lyfgenia or Casgevy: Who Will Lead the Sickle Cell Disease Treatment Space?
History has been created as the world captures the significance of the FDA’s approval of Casgevy (exa-cel), a collaboration between Vertex Pharmaceuticals and CRISPR Therapeutics, for the treatment of sickle cell disease (SCD). This groundbreaking therapy represents a long-awaited potential cure for the debilitatin...
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