Rare Disease

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Watershed Moment for Cell Therapies and Complicated Journey of Gene Therapies in Japan

In recent years, the development of cell and gene therapies has provided a new avenue for the treatment of rare disorders. This article will discuss the current and future scenarios of cell and gene therapies in rare disorders with cancer indications as an exception, in Japan. Cell therapy is a treatment in which l...

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Top Most Expensive Drugs in the US Healthcare Market
Top 12 Most Expensive Drugs in the US Healthcare Market

Drug pricing is one of the hottest topics in the healthcare segment. Several arguments have been put forward by people, governments, healthcare companies, and other organizations in favor of and against expensive medicines. Some of the drugs are so expensive that they are nearly out of reach of the common people. H...

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Introducing a New Era of Hemophilia Management Tools
Role of Mobile Technology in Hemophilia Management

The universality of mobile technology has proven to be extremely beneficial, specifically in recent years. The potential of improving medical care delivery, and the potential for instantaneous and two-way transfer of information has turned out to be a revolutionary step. The following article indicates the importan...

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artificial-intelligence-in-healthcare
Most Promising Applications of Artificial Intelligence (AI) in Healthcare Segment

Artificial Intelligence (AI), with its wide range of applications, is enhancing the speed and accuracy of businesses across various industries such as manufacturing, healthcare, finance, marketing, and several others. To take advantage, globally, companies, whether big or small, are actively adopting artificial int...

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Aslan Pharma – IQVIA collaboration; Reata’s kidney drug bardoxolone; Alzheimer’s Disease treatment update; Recordati to acquire EUSA

Aslan Pharmaceuticals enters into a strategic collaboration with IQVIA   ASLAN Pharmaceuticals announced the appointment of IQVIA Biotech, a provider of analytics, technology solutions, and clinical research services to the life sciences industry, as its preferred clinical research organisation for log...

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Another Failed NASH Drug; Takeda’s Dengue Shot; Innovent’s Cholangiocarcinoma Clinical Trial; TLX66 in AL Amyloidosis
TLX66 in AL Amyloidosis; Takeda’s Dengue Shot; Innovent’s Cholangiocarcinoma Clinical Trial; Another Failed NASH Drug

TLX66 Meets Study Objectives, Holding Out in AL Amyloidosis Telix Pharmaceuticals reported the results from the TRALA trial (Targeted Radiotherapy for AL Amyloidosis), a Phase I/IIa trial evaluating the safety and toxicity of TLX66 as the sole bone marrow conditioning agent prior to autologous hematopoietic stem...

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Rare Cancer Market | Soft Tissue Sarcoma Market | Multiple Myeloma Market | Glioblastoma Multiforme Market | Cholangiocarcinoma Market | Synovial Sarcoma Market
Rare Cancer Market: A Global Crusade on what is a ‘less common cancer’?

Cancer is often challenging, however, diagnosis of rare cancer poses extra difficulties. Of all the diagnosed cancers, approximately 22% of the cases are rare cancers. According to the US National Cancer Institute, a cancer rare cancers as those with an incidence of fewer than 15 cases per 100 000 per year. Rare...

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Rare Disease Market Drivers | Orphan Drugs
What are the Market Drivers Fueling the Rare Disease Market?

Rare diseases–also go by the name Orphan diseases–are the conditions that do not affect many individuals out there in one particular geographic area. Going deeper into the definition, it also means a lesser patient pool for a therapy developed for one identified rare condition. Unfavorable drug uptake would automat...

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Erythropoietic Protoporphyria Market Outlook
Emerging Research Continues To Transform Erythropoietic Protoporphyria Market Outlook

Lack of knowledge about conditions, situations, or body ailments that are unexplainable often scares people and leads to people jumping to conclusions or say myths that are not at all backed by science and logic. Myths are a seemingly convenient way to explain what the mind perceives as unexplainable.  This...

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Hypofibrinogenemia Market | Rare Bleeding Disorders
Hypofibrinogenemia Market: Limited Pipeline Therapies, Abundant Opportunities

Like troops at the forefront of any battle, our immune system continually marches to protect us from foreign elements and invaders, including bacteria, viruses, and others. Whenever with a swift wave of wind, something falls in our eyes, our immune system produces tears to get rid of the invader. Or at times when w...

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